Gene Therapy without using viruses to get genes to cells

Gene Therapy goal: deliver desired genes to cells to either cure disease or improve body functions such as stronger muscles. Gene therapy has the potential to enhance human performance and cure diseases.

Problem: Viruses used for gene delivery occasionally cause severe immune responses.

The novel lipid molecule created at UC Santa Barbara has a tree-shaped, nanoscale headgroup and displays unexpectedly superior DNA-delivery properties.

Background: Lipids are molecules with two parts, a water-liking “headgroup” and oily tails that assemble together to avoid water. Lipids, along with carbohydrates and proteins, constitute the main structural material of living cells.

logo

Don’t miss the latest future news

Subscribe and get a FREE Ebook